Skeletal Muscle as a Target for AAV Vector Delivery:

Lessons Learned from Hemophilia B and Pompe Disease

Katherine A. High, MD

Emeritus Professor, Pediatrics, Perelman School of Medicine,

University of Pennsylvania

Contact – Gloria Kiel-Gutierrez – gskiel@mednet.ucla.edu

Website: https://www.uclahealth.org/ortho/musculoskeletal-calendar