Development of Gene Therapy Strategies to Treat X-Linked Lymphoproliferative Diseases

Claire Booth, MB, BS, PhD

Professor, Gene Therapy & Pediatric Immunology, University College London

Immune Suppression Strategies for Clinical Re-Dosing of

AAV-Based Gene Therapies for Pediatric Disorders

Barry Byrne, MD, PhD

Associate Chair, Pediatrics, University of Florida

Gene Therapies that Target Gene Silencing or Splicing in Lymphocytes

Edvard Smith, MD, PhD

Professor, Molecular Genetics, Karolinska Institutet     – and –

Gene Therapies for Pediatric Blood Disorders

Stephano Rivella, PhD

Professor, Pediatrics, University of Pennsylvania, School of Medicine

RSVP – https://www.eventcreate.com/e/minisymposium

Carnesale Commons, Palisades Room